Multi-Company, Multi-Product Clinical Trials On The Cards For Rare Pediatric Diseases

Industry is guardedly optimistic about a new joint proposal from US and EU regulators for companies to test their drugs for rare pediatric diseases together in single multi-product studies.

Medication
US and EU regulatrs want companies to collaborate on drugs for rare pediatric diseases • Source: Shutterstock

Developers of medicines for rare diseases in children should consider the possibility of testing their products in multi-company, multi-product studies, according to a joint proposal by regulators in the US and the EU.

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